DM-1

DM-1

DM-1 Product List

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Clinical Drug Information

English NameResearch CodeHighest Development StageCompanyIndicationClinical Trial
Delpacibart eteddesiranAOC-1001; AOC 1001Phase 3 ClinicalAvidity Biosciences Inc
Myotonic Disorders; Genetic Diseases, Inborn; Musculoskeletal Diseases; Muscular Disorders, Atrophic; Myotonic Dystrophy; Muscular Atrophy; Heredodegenerative Disorders, Nervous System; Muscular Diseases; Neuromuscular Diseases; Nervous System Diseases; Muscular Dystrophies; Neurodegenerative Diseases; Myotonia
Details
Dyne-101Dyne101Phase 2 ClinicalDyne Therapeutics Inc
Myotonic Dystrophy
Details
ARO-DM1ARO-DM1Phase 2 ClinicalArrowhead Pharmaceuticals Inc
Myotonic Dystrophy
Details