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5-OMe-UTP dsRNA (400bp) Standard

5-OMe-UTP dsRNA (400bp) Standard Product List

  • Product Category

    Nucleic Acid (1)

  • Product Status

    Launched (1)

  • Species

    - (1)

  • Tag

    - (1)

  • Conjugate

    - (1)

Cat. No.SpeciesHostProduct DescriptionStructurePurityFeatureOrder Now
RES092-C09
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5-OMe-UTP dsRNA (400bp) Standard Add to Cart
Total: 1
  • 1

Clinical Drug Information

English NameResearch CodeHighest Development StageCompanyIndicationClinical Trial
Emixustat HydrochlorideACU-02; ACU-4429; ACU-4429 HClPhase 3 ClinicalAcucela IncAnetoderma; Geographic Atrophy; Stargardt Disease; Macular Degeneration; Diabetic Retinopathy
Details
LX-101LX-101Phase 3 ClinicalShanghai Langsheng Biological Technology Co LtdRetinal Dystrophies; Retinal Dysplasia; Retinal Degeneration
Details
HORA-RPE65 (Horama)HORA-RPE65Phase 2 ClinicalHorama SaLeber Congenital Amaurosis
Details
HG-004HG-004Phase 2 ClinicalHuiGene Therapeutics LtdLeber Congenital Amaurosis; Retinal Diseases
Details

Marketed Drug Information

English NameResearch CodeHighest Development StageCompanyEarliest Brand NameEarliest Approval CountryEarliest IndicationEarliest Approval CompanyEarliest Approval DateIndicationClinical Trial
Voretigene neparvovec-rzyl2SPI046IKD; rAAV.hRPE65v2; AAV2-hRPE65v2; SPKRPE-65; rAAV2-CBSB-hRPE65; AAV2.RPE65ApprovedThe Children'S Hospital Of PhiladelphiaLuxturnaUnited StatesRetinal DysplasiaSpark Therapeutics Inc2017-12-19Vision Disorders; Retinal Dystrophies; Leber Congenital Amaurosis; Retinal Dysplasia
Details
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  • Marketed Drug Information
  • Clinical Drug Information